Other content with the tag "Lysosomal storage disorders".

Evaluation of Lyso-Gb1 as a biomarker for Gaucher disease treatment outcomes using data from the Gaucher Outcome Survey
January 31, 2025

This study evaluates Lyso-Gb1 as a biomarker for monitoring treatment response in Gaucher disease (GD) patients, using real-world data from the Gau